Cell and Gene Therapy Center

  • Cell and Gene Therapy

    Cell and Gene Therapy Center

  • Cell and Gene Therapy

    Cell and Gene Therapy Center

  • Cell and Gene Therapy Center

    Cell and Gene Therapy Center

  • Cell and Gene Therapy Center

    Cell and Gene Therapy Center

  • Cell and Gene Therapy Center

    Cell and Gene Therapy Center

Cell and Gene Therapy Center

Welcome to the Cell and Gene Therapy Center

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Our laboratory, under the direction of Dr. Paola Leone, studies pediatric white matter diseases and characterizes mechanisms to repair white matter with the goal to prevent and treat disease in patients. Our work focuses on neurological diseases that can be treated using the latest gene transfer technologies and cell transplantation methods. You can learn more by watching the video below or our award-winning film, Little Heroes